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Adeno-Associated Virus-Mediated RNAi against Mutant Alleles Attenuates Abnormal Calvarial Phenotypes in an Apert Syndrome Mouse Model Journal article
Luo,Fengtao, Xie,Yangli, Wang,Zuqiang, Huang,Junlan, Tan,Qiaoyan, Sun,Xianding, Li,Fangfang, Li,Can, Liu,Mi, Zhang,Dali, Xu,Meng, Su,Nan, Ni,Zhenhong, Jiang,Wanling, Chang,Jinhong, Chen,Hangang, Chen,Shuai, Xu,Xiaoling, Deng,Chuxia, Wang,Zhugang, Du,Xiaolan, Chen,Lin. Adeno-Associated Virus-Mediated RNAi against Mutant Alleles Attenuates Abnormal Calvarial Phenotypes in an Apert Syndrome Mouse Model[J]. Molecular Therapy - Nucleic Acids, 2018, 13, 291-302.
Authors:  Luo,Fengtao;  Xie,Yangli;  Wang,Zuqiang;  Huang,Junlan;  Tan,Qiaoyan; et al.
Favorite | TC[WOS]:15 TC[Scopus]:15  IF:6.5/6.7 | Submit date:2020/09/16
Adeno-associated Virus  Apert Syndrome  Craniosynostosis  Fgfr2  Molecular Therapy  Rnai